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  • : Severe Combined Immunodeficiency

Severe Combined Immunodeficiency - 9 Studies Found

Completed : Stem Cell Gene Therapy to Treat X-Linked Severe Combined Immunodeficiency (XSCID)
: Severe Combined Immunodeficiency
: 2001-12-17
: Drug: Gene-Transduced Autologous CD34+ Stem Cells
Active, not recruiting : Gene Therapy for X-linked Severe Combined Immunodeficiency
: X-linked Severe Combined Immunodeficiency
: 2011-06-21
: Other: Gene transfer Single infusion of autologous CD34+ cells transduced with the self-inactivating (SI
Completed : Gene Transfer for X-Linked Severe Combined Immunodeficiency in Newly Diagnosed Infants
: Severe Combined Immunodeficiency Disease, X-linked
: 2012-01-13
:
  • Genetic: CL20-4i-EF/a-hyc-OPT

Completed : Gene Transfer for Severe Combined Immunodeficiency, X-linked (SCID-X1) Using a Self-inactivating (SIN) Gammaretroviral Vector
: Severe Combined Immunodeficiency
: 2010-05-21
: Biological: Gene transfer Three procedures: 1) Bone marrow harvest from the patient's posterior iliac cr
Active, not recruiting : Gene Therapy for X-linked Severe Combined Immunodeficiency (SCID-X1)
: X-linked Severe Combined Immunodeficiency
: 2010-07-29
: Genetic: Single infusion of autologous CD34+ cells transduced with the self-inactivating (SIN) gammaretroviral vector pSRS11.EFS.IL2RG.pre
Completed : Influences on Female Adolescents' Decisions Regarding Testing for Carrier Status of XSCID
: Severe Combined Immunodeficiency
: 2000-10-04
Completed : Lentiviral Gene Transfer for Treatment of Children Older Than Two Years of Age With X-Linked Severe Combined Immunodeficiency (XSCID)
:
  • X-linked Severe Combined Immunodeficiency
  • XSCID
  • : 2011-02-26
    :
    • Other: Gene-modified CD34+ Hematopoietic stem cells

Recruiting : Evaluation of Patients With Immune Function Abnormalities
: Immune System Diseases
: 2005-08-09
COMPLETED : Long Term Follow Up Of Patients Who Have Received Gene Therapy Or Gene Marked Products
: Severe Combined Immunodeficiency
: 2025-08-01
: Blood draw
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