Pyruvate Kinase Deficiency - 1 Studies Found
| COMPLETED |
: A Study of AG-348 in Adult Participants With Pyruvate Kinase (PK) Deficiency : Pyruvate Kinase Deficiency : 2025-08-02 : Participants with PK deficiency were randomized to either receive AG-348, 50 or 300 mg, as initial doses, BID for the Core Period (Week 24).At t |