Mucopolysaccharidosis Type VII - 4 Studies Found

Completed : Biomarker for Sly Disease
:
  • Mucopolysaccharidosis VII
  • Sly Disease : 2014-10-23
Completed : A Phase 3 Study of UX003 rhGUS Enzyme Replacement Therapy in Patients With MPS 7
:
  • MPS 7
  • Sly Syndrome
  • : 2014-08-22
    :
    • Drug: UX003 UX003 is a sterile
Active, not recruiting : A Long-Term Open-Label Treatment and Extension Study of UX003 rhGUS Enzyme Replacement Therapy in Subjects With MPS 7
:
  • Sly Syndrome
  • MPS VII
  • : 2015-04-22
    : Drug: UX003 UX003 is a sterile liquid buffered saline formulation of rhGUS that contains enzyme at a con
Active, not recruiting : An Open-Label Study of UX003-rhGUS Enzyme Replacement Treatment in MPS 7 Patients Less Than 5 Years of Age
:
  • Sly Syndrome
  • MPS VII
  • : 2015-04-12
    : Drug: UX003 Other Names:
    • recombinant human beta-glucoronidase