Mucopolysaccharidosis I - 57 Studies Found
| Enrolling by invitation |
: Extension Study Evaluating Long Term Safety and Activity of AGT-181 in Children With MPS I : : 2025-07-30 |
| Enrolling by invitation |
: Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I :
: 2014-09-03 : Drug: Intrathecal recombinant human alpha iduronidase Intrathecal recombinant human alpha iduronidase ev |
| Not yet recruiting |
: Study to Evaluate the Safety and Efficacy of Adalimumab in MPS I and II :
: 2017-05-11 :
|
| Completed |
: Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-318 in Subjects With MPS I : MPS I : 2016-02-29 : Biological: SB-318 A single dose of each of the three components of SB-318 [zinc finger nucleases (ZFN1, |
| Enrolling by invitation |
: Extension Study of AGT-181-102 to Evaluate Long Term Safety and Activity of AGT-181 : Mucopolysaccharidosis I : 2015-11-03 : Drug: AGT-181 intravenous infusion over 3-4 hours Ot |
| Terminated |
: Clinical Trial of Growth Hormone in MPS I, II, and VI :
: Drug: Somatropin (DNA origin) The study starting dose of Nutropin AQ® will be 0.48 mg/kg/week divid |
| Not yet recruiting |
: Parental Coping With Challenging Behavior in Mucopolysaccharidosis Type I-III :
: 2017-04-24 : Other: This is an observational study This is an observational study |
| Terminated |
: Study to Detect Unrecognized Mucopolysaccharidosis in Children Visiting Rheumatology, Hand or Skeletal Dysplasia Clinics :
|
| Completed |
: A Study to Test the Possibility of Cross Reaction Induced by the Idursulfase Drug to GSK2788723 : Mucopolysaccharidosis II : 2012-05-17 :
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