Lipidoses - 13 Studies Found Completed : Safety, Tolerability, PK, and Efficacy Evaluation of Repeat Ascending Doses of Olipudase Alfa in Pediatric Patients <18 Years of Age With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2014-11-07 : Drug: Olipudase alfa Pharmaceutical form: powder for concentrate for solution for infusion Route of admi Completed : A Long-Term Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2013-11-26 : Drug: GZ402665 Pharmaceutical form: Powder for concentrate Completed : Efficacy, Safety, Pharmacodynamic, and Pharmacokinetics Study of Olipudase Alfa in Patients With Acid Sphingomyelinase Deficiency : Sphingomyelin Lipidosis : 2013-11-26 : Drug: placebo (saline) Completed : SCH-58235 (Ezetimibe) to Treat Homozygous Sitosterolemia : Lipoidosis : 2002-09-10 : Drug: SCH-58235 Completed : Evaluation of Antioxidant Activity of Oral Lutein in Preterm and Term Newborn : Infant, Newborn, Diseases Other Lipid Storage Disorders : 2014-02-17 : Dietary Supplement: Lutein drops Completed : Biomarker for Niemann Pick Type C Disease : Niemann-Pick Disease Niemann-Pick Disease, Type C : 2011-03-01 Completed : The Natural History and Pathogenesis of Mucolipidosis Type IV : Mucolipidosis Type IV : 2001-05-04 Completed : Phase I Study of Retrovirally Mediated Transfer of the Human Glucocerebrosidase Gene Into Peripheral Blood Stem Cells for Autologous Transplantation in Patients With Type I Gaucher Disease : Gaucher's Disease : 1999-10-18 : Genetic: human glucocerebrosidase gene into autologous peripheral blood stem cells Completed : Phase II Study of Glucocerebrosidase in Patients With Gaucher Disease : Gaucher's Disease : 1999-10-18 : Drug: glucocerebrosidase Completed : Phase II Randomized Study of Alendronate Sodium for Osteopenia in Patients With Gaucher's Disease : Gaucher's Disease Osteopenia : 1999-10-18 : Drug: alendronate sodium Drug: calcium car Next >>>
