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  • : Hemoglobinuria

Hemoglobinuria - 42 Studies Found

Active, not recruiting : Paroxysmal Nocturnal Hemoglobinuria (PNH) Registry
: Paroxysmal Nocturnal Hemoglobinuria
: 2011-04-15
Completed : Eculizumab to Treat Paroxysmal Nocturnal Hemoglobinuria
: Paroxysmal Hemoglobinuria, Nocturnal
: 2005-08-11
: Drug: Eculizumab
Completed : Transfer of GPI-Linked Proteins to Transfused Patients With Paroxysmal Nocturnal Hemoglobinuria
: Paroxysmal Hemoglobinuria
: 2002-06-14
Completed : E07-001: Safety and Efficacy Extension Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients
: Paroxysmal Nocturnal Hemoglobinuria
: 2010-08-30
: Drug: Eculizumab Each vial contains 30 mL of 10 mg/mL eculizumab; dose of 900 mg intravenous every 14 da
Completed : A Treatment Study of ACH-0144471 in Patients With Paroxysmal Nocturnal Hemoglobinuria (PNH)
: Paroxysmal Nocturnal Hemoglobinuria (PNH)
: 2017-02-01
: Drug: ACH-0144471 ACH-0144471 will be administered to all patients enrolled in the study.
Completed : C07-001: Safety and Efficacy Study of Eculizumab in Paroxysmal Nocturnal Hemoglobinuria Patients
: Paroxysmal Nocturnal Hemoglobinuria
: 2010-08-30
: Biological: Eculizumab Subjects were treated with open label Eculizumab and following the dose described
Active, not recruiting : An Open-Label, Intrapatient, Dose-Escalation Study to Evaluate the Safety, Tolerability, Efficacy, Pharmacokinetics, and Pharmacodynamics of ALXN1210 Administered Intravenously to Patients With Paroxysmal Nocturnal Hemoglobinuria
: Paroxysmal Nocturnal Hemoglobinuria (PNH)
: 2015-11-02
:
  • Biological: Study Drug - ALXN1210

Completed : Study to Assess Safety, Efficacy, Pharmacokinetics, and Pharmacodynamics of RO7112689 in Healthy Volunteers and Participants With Paroxysmal Nocturnal Hemoglobinuria
: Paroxysmal Hemoglobinuria, Nocturnal
: 2016-11-01
:
  • Drug: RO7112689 RO7112689 will

Completed : Coversin in Paroxysmal Nocturnal Haemoglobinuria (PNH)
: Paroxysmal Nocturnal Haemoglobinuria (PNH)
: 2015-09-10
: Drug: Coversin Patients enrolled in this protocol will initially be treated with an ablating dose of Cov
Completed : Proof of Concept Study to Assess the Efficacy, Safety and Pharmacokinetics of LFG316 in Patients With Paroxysmal Nocturnal Hemoglobinuria
: Paroxysmal Nocturnal Hemoglobinuria PNH
: 2015-08-07
: Biological: LFG316 LFG316 will be administered to all patients enrolled in the study
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