Dysferlinopathy - 4 Studies Found

Completed : rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies
: Dysferlinopathy
: 2016-02-11
: Drug: rAAVrh74.MHCK7.DYSF.DV Biological/Vaccine: rAAVrh74.MHCK7.DYSF.DV Recombinant adeno-associated vir
Completed : Deflazacort in Dysferlinopathies
:
  • LGMD2B
  • Miyoshi Myopathy
  • Dysferlinopa
    : 2007-09-06
    :
    • Drug: deflazacort In the first
Active, not recruiting : Clinical Outcome Study for Dysferlinopathy
:
  • Dysferlinopathy
  • LGMD2B
  • Miyosh
    : 2012-08-28
Completed : Proteasomal Inhibition for Patients With Mis-sense Mutated Dysferlin
: Dysferlinopathy
: 2013-04-29
: Drug: Bortezomib Other Name: Velcade®