Diamond-Blackfan Anemia - 2 Studies Found

Completed : Magnetic Resonance Imaging (MRI) Assessments of the Heart and Liver Iron Load in Patients With Transfusion Induced Iron Overload
:
  • Hemoglobinopathies
  • Myelodysplastic Syndromes
  • Other Inherit
    : 2008-05-05
    : Drug: deferasirox Deferasirox up to 40mg/kg/day, PO, Dispersible tablets, taken once daily
Completed : Study of the Selective GlyT1 Inhibitor Bitopertin for Steroid-Refractory Diamond-Blackfan Anemia
: Steroid-refractory Diamond-Blackfan Anemia (DBA)
: 2025-08-02
: Dose Escalation: Monthly (every 4 weeks) up to a maximum dose of 60 mg bitopertin (5 mg, 10mg, 20mg, 40mg, 60mg).At each monthly (4 week) interv