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Aromatic L-amino Acid Decarboxylase Deficiency - 1 Studies Found
Estado | Estudiar |
Completed |
Nombre del estudio: A Phase I/II Clinical Trial for Treatment of Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Using AAV2-hAADC Condición: Aromatic L-amino Acid Decarboxylase (AADC) Deficiency Fecha: 2011-06-12 Intervenciones: Drug: gene therapy AAV2-hAADC viral vector will be injected into bilateral putamen by stereotactic surge |