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  • : Arginase Deficiency

Arginase Deficiency - 2 Studies Found

Completed : A Phase 1/2 Study of AEB1102 in Patients With Arginase I Deficiency
:
  • Arginase I Deficiency
  • Hyperargininemia

: 2015-06-29
: Drug: AEB1102 modified human arginase I Other Name:
Terminated : The NIH UNI Study: Urea Cycle Disorders, Nutrition and Immunity
:
  • Argininosuccinic Aciduria
  • Carbamoyl-Phosphate Synthase I Deficiency
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