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  • : Anemia, Hypoplastic, Congenital

Anemia, Hypoplastic, Congenital - 14 Studies Found

Completed : Pilot Study of Etanercept (Enbrel) in Children With Fanconi Anemia
: Fanconi Anemia
: 2009-08-24
: Drug: Etanercept All qualified subjects receive 24 weekly subcutaneous injections of Etanercept.
Completed : Microcephaly Genetic Deficiency in Neural Progenitors
: Microcephaly
: 2012-02-29
Completed : Lentiviral-mediated Gene Therapy of Fanconi Anemia Patients Subtype A
: Fanconi Anemia
: 2017-04-26
:
  • Procedure: IV administration of Genetically Engineered Hematopoietic Stem/Pr

Completed : Clinical Phase II Trial to Evaluate CD34+ Cells Mobilization and Collection in Patients With Fanconi Anemia for Subsequent Transduction With a Lentiviral Vector Carring FANCA Gene. FANCOSTEM-1
: Fanconi Anemia
: 2016-09-06
:
  • Drug: filgrastim G-CSF (12

Completed : Mobilization and Collection of Peripheral Blood Stem Cells in Patients With Fanconi Anemia Using G-CSF and Plerixafor
: Fanconi Anemia
: 2016-02-05
:
  • Drug: G-CSF D1 to D4 : Injecti

Enrolling by invitation : Unrelated HSCT in Patients With Fanconi Anemia
: Fanconi Anemia
: 2012-10-19
: Biological: CD34+ selected cells Compassionate treatment of Fanconi Anemia patients with unrelated bone
Completed : Quercetin in Children With Fanconi Anemia; a Pilot Study
: Fanconi Anemia
: 2012-07-25
: Drug: Quercetin (dietary supplement) Quercetin will be given orally on a twice a day schedule starting w
Recruiting : Gene Therapy for Fanconi Anemia
: Fanconi Anemia
: 2011-03-16
:
  • Procedure: Bone Marrow Aspiration

Completed : Multicenter Transplant Study for Fanconi Anemia
: Fanconi Anemia
: 2010-03-05
:
  • Drug: Chemotherapy Busulfan 0.

Active, not recruiting : Hematopoietic Stem Cell Transplant for Fanconi Anemia
: Fanconi Anemia
: 2009-05-20
: Device: CliniMACs device Donor Peripheral blood progenitor cells will use CD34+ selection with the use o
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