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  • : Acute Intermittent Porphyria

Acute Intermittent Porphyria - 14 Studies Found

Completed : Observational Study of Acute Intermittent Porphyria Patients
: Acute Intermittent Porphyria
: 2014-02-27
Not yet recruiting : Dental Health, Diet, Inflammation and Biomarkers in Patients With Acute Intermittent Porphyria(AIP)
: Acute Intermittent Porphyria
: 2012-06-05
Completed : A Phase 1 Study of ALN-AS1 in Patients With Acute Intermittent Porphyria (AIP)
: Acute Intermittent Porphyria
: 2015-05-19
:
  • Drug: ALN-AS1 Single or multip

Completed : Phase I Gene Therapy Clinical Trial Using the Vector rAAV2/5-PBGD for the Treatment of Acute Intermittent Porphyria
: Acute Intermittent Porphyria
: 2014-02-28
:
  • Genetic: rAAV2/5-PBGD vector dosage 1

Enrolling by invitation : A Study to Evaluate Long-term Safety and Clinical Activity of ALN-AS1 in Patient With Acute Intermittent Porphyria (AIP)
: Acute Intermittent Porphyria
: 2016-10-28
: Drug: ALN-AS1 ALN-AS1 by subcutaneous (SC) injection
Completed : Porphozym in the Treatment of Acute Attacks in AIP
: Acute Intermittent Porphyria
: 2007-01-04
: Drug: recombinant human porphobilinogen deaminase (Porphozym)
Enrolling by invitation : Acute Porphyria Biomarkers
:
  • Acute Intermittent Porphyria
  • Hereditary Coproporphyria
  • : 2016-10-13
    : Drug: Hemin Hemin will be administered under a separate protocol or for clinical treatment, and samples
Completed : Clinical Diagnosis of Acute Porphyria
:
  • Hereditary Coproporphyria (HCP)
  • Acute Intermittent Porphyria (A
    : 2012-02-16
Completed : Controlled Trial of Panhematin in Treatment of Acute Attacks of Porphyria
: Acute Porphyrias
: 2014-06-25
:
  • Biological: Panhematin
  • Other: Placebo

Completed : Longitudinal Study of the Porphyrias
:
  • Acute Porphyrias
  • Cutaneous Porphyrias

: 2012-02-13
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