Leber Hereditary Optic Neuropathy - 21 Studies Found
| Completed |
: Gene Therapy Clinical Trial for the Treatment of Leber's Hereditary Optic Neuropathy Associated With ND4 Mutations : Leber Hereditary Optic Neuropathy (LHON) : 2025-08-01 : The starting dose is 1.5E9 vg, 0.05 mL eye/dose.Dose Escalation:If drug-related dose-limiting toxicity (DLT) events are observed |