Mucopolysaccharidoses - 19 Studies Found

Active, not recruiting : Longitudinal Study of Bone Disease in Children With Mucopolysaccharidoses (MPS) I, II, and VI
: Mucopolysaccharidoses
: 2011-11-11
Completed : Iduronate-2-sulfatase Enzyme Replacement Therapy in Mucopolysaccharidosis II (MPS II)
: Mucopolysaccharidosis II
: 2003-09-29
:
  • Biological: Iduronate-2-sulfatase enzyme replacement therapy

Completed : Natural History Study of Patients With MPS IIIA
: Mucopolysaccharidosis IIIA
: 2016-04-15
No longer available : An Open-Label Treatment Protocol With UX003 rhGUS Enzyme Replacement Therapy for an Advanced Stage MPS 7 Patient
: Mucopolysaccharidosis Type 7
: 2014-03-24
: Drug: UX003 Open Label Other Names:
Completed : Ascending Dose Study of Genome Editing by the Zinc Finger Nuclease (ZFN) Therapeutic SB-913 in Subjects With MPS II
: Mucopolysaccharidosis II
: 2017-01-13
: Biological: SB-913 Single dose of each of the 3 components of SB-913: ZFN1, ZFN2 and hIDS Donor
Completed : To Evaluate the Safety and Efficacy of GC1111 (Recombinant Human Iduronate-2-sulfatase) in Hunter Syndrome Patients
: Mucopolysaccharidosis II
: 2011-02-22
:
  • Drug: GC1111_0.5mg/kg
  • Drug: GC1111_1.0mg/k
Not yet recruiting : Study of Idursulfase-beta (GC1111) in Hunter Syndrome
: Mucopolysaccharidosis II
: 2016-01-17
:
  • Biological: idursulfase beta I
Completed : Safety and Dose Ranging Study of Insulin Receptor MoAb-IDS Fusion Protein in Patients With Hunter Syndrome
: Mucopolysaccharidosis II
: 2014-10-02
: Drug: AGT-182 Recombinant HIRMAb-IDS
Completed : Mucopolysaccharidosis (MPS) VI Clinical Surveillance Program (CSP)
: Mucopolysaccharidosis VI (MPS VI, Maroteaux-Lamy Syndrome)
: 2005-09-13
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