Leukodystrophy - 35 Studies Found

Enrolling by invitation : Long-term Follow-up of Subjects With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Product
:
  • Cerebral Adrenoleukodystrophy (CALD)
  • Adre
    : 2016-02-17
    : Other: Safety and efficacy assessments Vector copy number (VCN) measurement, safety evaluations, disease
Completed : Exercise Study of Function and Pathology for Women With X-linked Adrenoleukodystrophy
: X-linked Adrenoleukodystrophy
: 2012-05-07
: Behavioral: exercise training The exercise program uses a local Curves® gym to provide an individua
Completed : Observational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)
:
  • X-Linked Adrenoleukodystrophy (X-ALD)
  • Adrenoleukodystrophy
    : 1999-10-18
    :
    • Drug: glyceryl trierucate
    • Drug: glyceryl t
Not yet recruiting : Early Diagnosis Of Childhood Cerebral ALD
: Adrenoleukodystrophy
: 2016-10-25
Completed : Autologous Hematopoietic Stem Cell Gene Therapy for Metachromatic Leukodystrophy and Adrenoleukodystrophy
:
  • Metachromatic Leukodystrophy
  • Adrenoleukodystrophy

: 2015-08-12
: Genetic: transduced CD34+ hematopoietic stem cell Autologous hematopoietic stem cells (HSCs) collected f
Active, not recruiting : MD1003-AMN MD1003 in Adrenomyeloneuropathy
:
: 2025-08-02
Completed : A Clinical Trial for AMN: Validation of Biomarkers of Oxidative Stress, Efficacy and Safety of a Mixture of Antioxidants
: Adrenomyeloneuropathy
: 2011-11-28
:
  • Drug: N-acetylcysteine N-acety
Completed : UCB Transplant of Inherited Metabolic Diseases With Administration of Intrathecal UCB Derived Oligodendrocyte-Like Cells
:
  • Adrenoleukodystrophy
  • Batten Disease
  • Adrenoleukodystrophy
  • Metachromatic Leukodystrophy
  • : 2006-09-29
    :
    • Drug: Clofarabine days -7 thro
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