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Glycogen Storage Disease Type 2 - 22 Studies Found

Status Study
Completed Study Name: Observational Study for Subjects With Pompe Disease Undergoing Immune Modulation Therapies
Condition: Pompe Disease
Date: 2011-09-15
Interventions:
  • Drug: Rituximab Clinically pre
Completed Study Name: Pompe Disease Registry
Condition:
  • Glycogen Storage Disease Type II
  • Pompe Di
    Date: 2005-09-30
Completed Study Name: Safety Study of Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase to Treat Pompe Disease
Condition: Pompe Disease
Date: 2009-07-13
Interventions:
  • Drug: rAAV1-CMV-GAA (study agent) Administration

Not yet recruiting Study Name: Re-administration of Intramuscular AAV9 in Patients With Late-Onset Pompe Disease
Condition: Pompe Disease
Date: 2014-09-11
Interventions:
  • Genetic: Recombinant Adeno-Associated Virus Acid Alpha-Glucosidase

Completed Study Name: Determination of CRIM Status and Longitudinal Follow-up of Individuals With Pompe Disease
Condition: Pompe Disease
Date: 2012-08-13
Interventions: Other: Observational This is a longitudinal study focused on the emerging natural history of Infantile P
Recruiting Study Name: Pompe Disease QMUS and EIM
Condition: Pompe Disease
Date: 2016-04-11
Interventions:
  • Device: Muscle ultrasound Ultr
Completed Study Name: Screening Protocol to Evaluate Acid Alpha-Glucosidase (GAA) Activity and GAA Gene Mutations in Patients With Late Onset Pompe Disease
Condition: Pompe Disease
Date: 2005-06-03
Completed Study Name: Screening for Early Detection and Prevention of Pompe Disease in Israel Using Tandem Mass Spectrometry
Condition: Pompe Disease
Date: 2011-07-07
Interventions: Other: Drawing blood spots from Newborns Dry blood spots would be taken for determination of Alpha Gluco
Completed Study Name: CPAP for Infantile Pompe Disease
Condition: Pompe Disease
Date: 2015-03-21
Interventions: Procedure: continuous positive airway pressure CPAP training for muscle strength
Completed Study Name: Immune Modulation Therapy for Pompe Disease
Condition: Pompe Disease
Date: 2015-08-10
Interventions:
  • Drug: Rituximab
  • Drug: intravenous immune g
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