Search for Clinical Trial Results

Brain Diseases, Metabolic - 19 Studies Found
Status | Study |
Completed |
Study Name: Bioequivalence Study of Two Nitisinone Formulations Compared to Orfadin Condition: Hereditary Tyrosinemia, Type I Date: 2016-04-20 Interventions:
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Completed |
Study Name: Bioequivalence Study of Two Oral Nitisinone Formulations to Treat Hereditary Tyrosinemia (HT-1) Condition: Hereditary Tyrosinemia, Type I Date: 2016-04-21 Interventions:
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Completed |
Study Name: Bioavailability Food-Effect Study of an Oral Nitisinone Formulation to Treat Hereditary Tyrosinemia (HT-1) Condition: Hereditary Tyrosinemia, Type I Date: 2016-04-21 Interventions: Drug: Nitisinone A single oral dose of Nitisinone 10 mg Tablet will be administered. |
Not yet recruiting |
Study Name: The Effectiveness of Kuvan in Amish PKU Patients Condition: Phenylketonuria Date: 2016-01-26 Interventions:
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Not yet recruiting |
Study Name: Trial of Dichloroacetate in Pyruvate Dehydrogenase Complex Deficiency: Condition: Pyruvate Dehydrogenase Complex Deficiency Date: 2015-11-17 Interventions:
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Not yet recruiting |
Study Name: Simplified Diet Approach in Phenylketonuria Condition: Phenylketonuria Date: 2015-09-17 Interventions: Behavioral: Dietary Protein Counting and Free Fruits and Vegetables Subjects will be educated on new sim |
Completed |
Study Name: Intervention and Outcomes in Duarte Galactosemia Condition: Duarte Galactosemia Date: 2015-08-06 |
Active, not recruiting |
Study Name: A Phase 3 Substudy to Evaluate Executive Function in Adults With PKU Who Are Participating in the Phase 3 Study, 165-302 Condition: Phenylketonuria Date: 2015-06-03 Interventions: Other: Administration of CANTAB and Subject Global Assessment At designated visits, subject will perform |
Completed |
Study Name: Testing of Four Home Phenylalanine Monitoring Prototype Devices Condition: Phenylketonurias Date: 2015-05-13 |