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  • : Anemia, Diamond-Blackfan

Anemia, Diamond-Blackfan - 25 Studies Found

Terminated : Multi-Center Study of Iron Overload: Survey Study (MCSIO)
:
  • Sickle Cell Disease
  • Thalassemia
  • Diam
    : 2013-07-30
Terminated : Allo-HCT MUD for Non-malignant Red Blood Cell (RBC) Disorders: Sickle Cell, Thal, and DBA: Reduced Intensity Conditioning, Co-tx MSCs
:
  • Sickle Cell Disease
  • Thalassemia
  • Diam
    : 2009-08-12
    :
    • Procedure: Bone marrow transplantation

Terminated : Multi-Center Study of Iron Overload: Pilot Study
:
  • Sickle Cell Disease
  • Thalassemia
  • Diam
    : 2010-04-30
Completed : Partially Matched Stem Cell Transplantation for Patients With Refractory Severe Aplastic Anemia or Refractory Cytopenias
:
  • Anemia, Aplastic
  • Amegakaryocytic Thrombocytopenia
  • : 2005-10-24
    : Device: Allogeneic stem cell transplant Participants will receive a reduced intensity conditioning regim
Completed : Stem Cell Transplant for Bone Marrow Failure Syndromes
:
  • Diamond-Blackfan Anemia
  • Kostmann's Neutropenia
  • Procedure: Stem cell transplant

Completed : Expanded Access of Deferasirox to Patients With Congenital Disorders of Red Blood Cells and Chronic Iron Overload
:
  • Thalassemia
  • Sickle Cell Disease
  • Diam
    : 2005-10-06
    : Drug: Deferasirox 125 mg, 250 mg and 500 mg tablets. Dosage was calculated based on participant's body w
Completed : Study of Deferasirox in Iron Overload From Beta-thalassemia Unable to be Treated With Deferoxamine or Chronic Anemias
:
  • Beta-thalassemia
  • Myelodysplastic Syndromes
  • Fanconi Syndrom
    : 2003-06-03
    : Drug: Deferasirox
Completed : Alemtuzumab, Fludarabine, and Busulfan Followed By Donor Stem Cell Transplant in Treating Young Patients With Hematologic Disorders
:
  • Congenital Amegakaryocytic Thrombocytopenia
  • Diamond-blackfan Anemia : 2006-03-09
    :
    • Biological: alemtuzumab
    • Drug: busulfan

Active, not recruiting : Stem Cell Transplant for Hemoglobinopathy
:
  • Sickle Cell Disease
  • Thalassemia
  • Severe Congenital Neutrope
    : 2005-09-12
    :
    • Drug: Busulfan, Fludarabine, ATG, TLI

Completed : Busulfan, Antithymocyte Globulin, and Fludarabine Followed By a Donor Stem Cell Transplant in Treating Young Patients With Blood Disorders, Bone Marrow Disorders, Chronic Myelogenous Leukemia in First Chronic Phase, or Acute Myeloid Leukemia in First Remission
:
  • Congenital Amegakaryocytic Thrombocytopenia
  • Diamond-blackfan Anemia : 2006-03-21
    :
    • Biological: anti-thymocyte globulin
    • Drug:

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