Amyloid Neuropathies - 25 Studies Found

Completed : Biomarker for Patients With Transthyretin-Related Familial Amyloidotic Polyneuropathy
:
  • Metabolic Diseases
  • Amyloid Neuropathies
  • TTR-mediated Amyloidosis
  • Amyloidosis, Hereditary
  • : 2013-10-09
    :
    • Drug: patisiran (ALN-TTR02) ad
Available : Expanded Access Protocol of Patisiran for Patients With Hereditary ATTR Amyloidosis (hATTR)
:
  • TTR-mediated Amyloidosis
  • Amyloidosis, Hereditary
  • : 2016-10-18
    : Drug: patisiran (ALN-TTR02) patisiran (ALN-TTR02) administered by intravenous (IV) infusion
Completed : ENDEAVOUR: Phase 3 Multicenter Study of Revusiran (ALN-TTRSC) in Patients With Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
:
  • Transthyretin (TTR) Mediated Familial Amyloidotic Cardiomyopathy (FAC)
  • Amyloidosis, Heredita
    : 2014-12-12
    :
    • Drug: Revusiran (ALN-TTRSC)
    • Drug: Sterile

Completed : The Effect of Diflunisal on Familial Transthyretin Amyloidosis
: Amyloidosis
: 2011-09-09
: Drug: Diflunisal Film-coated tablet, 250 mg twice daily, orally for approximately 2 years
Completed : Safety, Efficacy and Pharmacokinetics of Doxycycline Plus Tauroursodeoxycholic Acid in Transthyretin Amyloidosis
: Transthyretin Amyloidosis
: 2010-07-27
: Drug: Doxycycline + Tauroursodeoxycholic acid doxycycline 100 mg twice a day for 12 months; tauroursodeo
Completed : Transthyretin-Associated Amyloidoses Outcome Survey (THAOS)
:
  • Transthyretin Mutations
  • Transthyretin Amyloidosis

: 2008-02-25
: Other: None. Observational Study.
Completed : Screening for the Transthyretin-Related Familial Amyloidotic Small Fiber Polyneuropathy
:
  • Polyneuropathies
  • Amyloidosis
  • Amyloid
    : 2012-10-09
Completed : The Effects of Fx-1006A on Transthyretin Stabilization and Clinical Outcome Measures in Patients With Non-V30M Transthyretin Amyloidosis
: Transthyretin-associated Amyloidosis With Polyneuropathy
: 2008-02-27
: Drug: Fx-1006A During Part 1, patients will receive Fx-1006A 20mg soft gelatin capsules once daily (at t
Completed : Safety and Efficacy Study of Doxycycline/UrsoDeoxyCholicAcid on Disease Progression in ATTR Amyloidosis
:
  • Transthyretin Amyloidosis
  • Cardiomyopathy

: 2012-04-19
:
  • Drug: Doxycycline 200 mg/day (
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