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  • : Adenosine Deaminase Deficiency

Adenosine Deaminase Deficiency - 18 Studies Found

Completed : MND-ADA Transduction of CD34+ Cells From Children With ADA-SCID
: Severe Combined Immunodeficiency
: 2008-11-19
: Biological: ADA gene transfer Autologous CD34+ cells transduced with the retroviral vector MND-ADA, carr
Completed : Gene Transfer Therapy for Severe Combined Immunodeficieny Disease (SCID) Due to Adenosine Deaminase (ADA) Deficiency
: Severe Combined Immunodeficiency Syndrome
: 2001-06-27
: Drug: CD34+ cells transduced with ADA retrovir
No longer available : Emergency Use of Adoptive Immunotherapy With CMV-Specific T Cells After Donor Bone Marrow Transplant of an Infant With Immunodeficiency Syndrome and CMV Infection
:
  • Infection
  • Precancerous/Nonmalignant Condition

: 2007-10-19
:
  • Biological: therapeutic allogeneic lymphocytes

Completed : Patients Treated for SCID (1968-2010)
:
  • SCID
  • ADA-SCID
  • XSCID
  • : 2011-04-29
Completed : Natural History Study of SCID Disorders
:
  • SCID
  • Leaky SCID
  • Omenn Syndrome
  • Drug: ADA PBSC
  • Drug: ADA Umbilical Cord Bl

Recruiting : The Role of Bacteria and Genetic Variations in Cystic Fibrosis
: Lung Diseases
: 2006-07-13
Enrolling by invitation : Molecular and Clinical Studies of Primary Immunodeficiency Diseases
: Immunologic Deficiency Syndrome
: 2000-09-30
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